Spending $95m to speed up the anaemia project’s path to approval could be worth the investment for Astrazeneca.
Autolus leads winners in spite of scepticism over its CAR-T, and gene therapies disappoint.
Launch could be trickier than approval, not least because of problems diagnosing patients with primary haemophagocytic lymphohistiocytosis.
Swedish Orphan Biovitrum made waves yesterday by getting its rare disease asset emapalumab into the Ash late-breakers – and bagging approval soon afterwards.
Pain drugs look like they could face different outcomes, while targeted cancer agents will have a big month. Two biosimilar decisions also await.
Roche's Hemlibra has impressed, but uptake might not be as fast as some hope.