October 17, 2018 Krystal gets a flying start in epidermolysis bullosa gene therapy Krystal Biotech shares have surged 53% so far this week on gene therapy data in two patients, but rivals are waiting in the wings.
August 14, 2018 Amryt awaits crucial readout as it prepares rare disease push A looming interim analysis could make Amryt a player in epidermolysis bullosa – and boost its deal-making ambitions.
